Welcome to the website of the DMD Genetic Therapy Group

For Parents of Duchenne Muscular Dystrophy patients we have created a special website, written in a non-scientific language. This website can be found under INFORMATION FOR PARENTS (available in Dutch and English).

The DMD Genetic Therapy Group

We hope you find all the information you are looking for on our website. If not please do not hesitate to contact us.

A video has been created to show a “bit more behind the scene footage” of our work in Leiden and tells a bit more about exon skipping and the DMD disease.

Please have a look!

What’s hot in the research field?

Information on new developments in the genetic therapy field

Technology & development

Background information about exon skipping and biomarkers  

Applicability of exon skipping

Exon skipping for deletions, duplications or point mutations

Do you have a question about DMD or do you want to get in contact with Prof. dr. Annemieke Aartsma-Rus? Please leave a comment on the contact page.