Skip to content
Exon skipping
DMD Genetic Therapy group Leiden
Home
What’s hot in the research field?
Givinostat
Blog on CRISPR technology
Translarna
Background of the disease
Dystrophin protein
Reading frame
Splicing
Technology & Development
Exon skipping
Biomarkers
Applicability
Exon skipping for deletions
Exon skipping for duplications
Exon skipping for point mutations
Information for parents
The DMD Genetic Therapy group Leiden
Group members
Funding for research
Disclosures
News from the group
Publications
Relevant links
Contact
Givinostat
HOW DOES GIVINOSTAT WORK?
Explained by Annemieke Aartsma-Rus.
